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| Issue Date | Title | Author(s) | Type | Access Type |
|---|---|---|---|---|
| 2015 | Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study | Suhr, O.; Coelho, T.; Buades, J.; Pouget, J.; Conceicao, I.; Berk, J.; Schmidt, H.; Waddington-Cruz, M.; Campistol, J.; Bettencourt, B.; Vaishnaw, A.; Gollob, J.; Adams, D. | article | ![]() |


