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Repositório Científico do Centro Hospitalar do Porto
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Issue Date
Title
Author(s)
Type
Access Type
2013
Long-term effects of tafamidis for the treatment of transthyretin familial amyloid polyneuropathy
Coelho, T.
;
Maia, L.
;
Martins-Silva, A.
;
Cruz, M.
;
Planté-Bordeneuve, V.
;
Suhr, O.
;
Conceição, I.
;
Schmidt, H.
;
Trigo, P.
;
Kelly, J.
;
Labaudinière, R.
;
Chan, J.
;
Packman, J.
;
Grogan, D.
article
2015
Efficacy and safety of patisiran for familial amyloidotic polyneuropathy: a phase II multi-dose study
Suhr, O.
;
Coelho, T.
;
Buades, J.
;
Pouget, J.
;
Conceicao, I.
;
Berk, J.
;
Schmidt, H.
;
Waddington-Cruz, M.
;
Campistol, J.
;
Bettencourt, B.
;
Vaishnaw, A.
;
Gollob, J.
;
Adams, D.
article
2017
Trial design and rationale for APOLLO, a Phase 3, placebo-controlled study of patisiran in patients with hereditary ATTR amyloidosis with polyneuropathy
Adams, D.
;
Suhr, O.
;
Dyck, P.
;
Litchy, W.
;
Leahy, R.
;
Chen, J.
;
Gollob, J.
;
Coelho, T.
article
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Author
3
Coelho, T.
2
Adams, D.
2
Gollob, J.
2
Schmidt, H.
1
Berk, J.
1
Bettencourt, B.
1
Buades, J.
1
Campistol, J.
1
Chan, J.
1
Chen, J.
.
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Subject
2
Patisiran
2
Polyneuropathy
1
APOLLO
1
Clinical trial
1
Genetic mutation
1
hATTR amyloidosis
1
Hereditary disease
1
Methods
1
mNIS+7
1
Phase II
.
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Date issued
1
2017
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2015
1
2013